transforming pediatric health care

Nephrology

Case study: siRNA therapy enables kidney-only transplant in child with rare PH1

Primary hyperoxaluria type 1 (PH1) is a rare genetic disorder that causes excess oxalate, leading to kidney failure and systemic damage. While liver transplant is the only cure, FDA-approved therapies are making kidney-only transplants a viable option.

Nephrology

How Glofil tests and DEXA scans help improve outcomes and care for children

Nephrology

Bringing acute care nephrology services to the NICU

Care of neonates with renal failure after birth remains a significant clinical challenge. Decisions related to providing dialysis in a newborn relies on a partnership between the parents and treatment team, including nephrologists and neonatologists.

Nephrology

NCT05299554

A Phase 3 Open-label Extension Study to Evaluate the Long-term Safety and Tolerability of Chronocort in the Treatment of Participants Aged 16 Years and Over with Congenital Adrenal Hyperplasia.

Nephrology

NCT04741646

Nephrology

Nephrology

NCT04064827